Niemann Pick disease type C (Version: )

Relevant disorders: R380, GT179, TP519
Signed off date: 12 Aug 2026
Panel types: GMS Rare Disease, GMS signed-off
2 green entities
Entity ratingEntityMode of inheritanceMode of pathogenicityTags
Green
BIALLELIC, autosomal or pseudoautosomalN/AN/A
Green
BIALLELIC, autosomal or pseudoautosomalN/AN/A